Leigh Disease - 5 Studies Found

Completed : Safety and Efficacy Study of EPI-743 in Children With Leigh Syndrome
: Leigh Syndrome
: 2012-11-01
:
  • Drug: Placebo
  • Drug: EPI-743 15 mg/kg
Enrolling by invitation : Long-Term Safety and Efficacy Evaluation of EPI-743 in Children With Leigh Syndrome
: Leigh Syndrome
: 2014-08-21
: Drug: EPI-743 EPI-743 is a quinone oxidation product of alpha tocotrienol
Completed : A Dose-escalating Clinical Trial With KH176
:
  • MELAS
  • LHON
  • Leigh Syndrome : 2015-04-19
    :
    • Drug: KH176
    • Drug: placebo
Enrolling by invitation : Tissue Sample Study for Mitochondrial Disorders
:
  • Mitochondrial Disorders
  • Mitochondrial Disease
  • Melas
    • <
    : 2012-08-31
Active, not recruiting : EPI-743 for Mitochondrial Respiratory Chain Diseases
: Mitochondrial Diseases
: 2011-06-07
: Drug: EPI-743 EPI-743 is administered as a dose escalation from 50 mg bid to 100 mg tid