Mucopolysaccharidosis I - 101 Studies Found Enrolling by invitation : Long-Term Safety and Clinical Outcomes of Idursulfase IT and Elaprase Treatment in Pediatric Patients With Hunter Syndrome That Have Completed Study HGT-HIT-094 : Hunter Syndrome : 2015-04-01 : Drug: Idursulfase-IT Patients will receive idursulfase-IT treatment once every 28 days at a dose of 10 m Completed : Screening Study to Identify Pediatric Patients With Hunter Syndrome Who Demonstrate Evidence of Central Nervous System (CNS) Involvement and Who Are Currently Receiving Treatment With Elaprase® : Hunter Syndrome : 2009-07-09 : Behavioral: Neurobehavioral testing Active, not recruiting : Study of Intrathecal Idursulfase-IT Administered in Conjunction With Elaprase® in Pediatric Patients With Hunter Syndrome and Early Cognitive Impairment : Hunter Syndrome : 2014-01-17 : Biological: idursulfase-IT 10m Active, not recruiting : Extension of HGT-HIT-045 Evaluating Long-Term Safety and Clinical Outcomes of Idursulfase (IT)in Conjunction With Elaprase in Pediatric Patients With Hunter Syndrome and Cognitive Impairment : Hunter Syndrome : 2011-12-15 : Drug: Idursulfase-IT Idursulfase-IT administered once monthly at the dose used in study HGT-HIT-045 via Completed : Safety and Efficacy of Hunterase : Hunter Syndrome : 2012-07-16 : Biological: Hunterase once weekly, 0.5mg/kg IV infusion Completed : Observational Study to Evaluate Neurodevelopmental Status in Pediatric Patients With Hunter Syndrome (MPS II) : Mucopolysaccharidosis (MPS) Hunter Syndrome : 2013-03-12 Recruiting : Biomarker for Hunter Disease : Lysosomal Storage Diseases Hunter Disease Mucopolysaccharidosis I Mucopolysaccharidosis II : 2017-05-11 : Drug: Adalimumab Injection [Humira] Terminated : Clinical Trial of Growth Hormone in MPS I, II, and VI : Mucopolysaccharidosis I Mucopolysaccharidosis II : 2008-09-08 : Drug: Somatropin (DNA origin) The study starting dose of Nutropin AQ® will be 0.48 mg/kg/week divid Terminated : Mucopolysaccharidosis (MPS) I, II, and VI Screening in a High-Risk Population With Previous Surgical Repair or Presence of Inguinal and/or Umbilical Hernia in Combination With Pediatric ENT Surgery (The HATT Project) : Mucopolysaccharidosis Mucopolysaccharidosis I : 2014-03-20 <<< Previous | Next >>>