Hemophilia B - 25 Studies Found
| NOT_YET_RECRUITING |
: Safety and Efficacy Clinical Study of Severe Hemophilia B Treatment With KL001 : Hemophilia B Without Inhibitor : 2024-11-22 : Subjects will be dosed with single dose of KL001 at 2.5x10^12 vg/kg. |
| RECRUITING |
: Study of the Safety, Pharmacodynamics and Efficacy of ANB-002 in Patients With Hemophilia B (SAFRAN) : Hemophilia B : 2024-11-22 : Adeno-associated viral vector carrying the FIX gene single infusion at dose 1. |
| RECRUITING |
: Efficacy and Safety of CSL222 (Etranacogene Dezaparvovec) Gene Therapy in Adults With Hemophilia B With Pretreatment Adeno-associated Virus Serotype 5 (AAV5) Neutralizing Antibodies (Nabs) : Hemophilia B : 2024-11-22 : Administered as a single IV infusion. |
| RECRUITING |
: A Study of SerpinPC in Participants With Hemophilia B (HemB) With Inhibitors : Hemophilia B With Inhibitor : 2024-11-22 : Administered as SC injection. |
| RECRUITING |
: An Observational Cohort Study to Characterize the Effectiveness and Safety of HEMGENIX� in Patients With Hemophilia B : Hemophilia B : 2024-11-22 : HEMGENIX is a gene therapy medicinal product that aims to deliver a factor IX (FIX) gene expression cassette to the liver of patients with hemophilia |