Oculopharyngeal Muscular Dystrophy - 10 Studies Found
Recruiting |
: Screening in Oculopharyngeal Muscular Dystrophy : Oculopharyngeal Muscular Dystrophy : 2016-08-19 :
|
Not yet recruiting |
: Natural History Study of Oculopharyngeal Muscular Dystrophy : Oculopharyngeal Muscular Dystrophy : 2017-05-16 : Other: Non-interventional study Non-interventional study |
Not yet recruiting |
: Effect of Aerobic Training in Patients With Oculopharyngeal Muscular Dystrophy : Oculopharyngeal Muscular Dystrophy : 2014-06-04 : Behavioral: Exercise Ten weeks of home-training on a cycle ergometer 3 times a week for 30 minutes. |
Completed |
: Treatment of Dysphagia in Oculopharyngeal Muscular Dystrophy by Autologous Transplantation of Myoblasts : Muscular Dystrophy, Oculopharyngeal : 2008-10-15 : Procedure: Autologous myoblasts transplantation and myotomy Graft of autologous cell muscles (myoblasts) |
Completed |
: Safety Tolerability and Efficacy Study of Cabaletta to Treat Oculopharyngeal Muscular Dystrophy (OPMD) Patients : Oculopharyngeal Muscular Dystrophy : 2013-12-08 : Drug: Cabaletta |
Active, not recruiting |
: Continuation Protocol to Protocol BBCO-001 : Muscular Dystrophy, Oculopharyngeal (OPMD) : 2014-12-25 : Drug: Cabaletta 30gr Cabaletta 30 g for IV infusion administered every week over an additional 52 weeks |
Active, not recruiting |
: Dysphagia in Oculopharyngeal Muscular Dystrophy (OPMD)- Evaluation, Endoscopic Examination of Swallowing, Treatment and Long Term Follow up : Dysphagia : 2010-07-21 : Procedure: Upper esophageal sphincter myotomy Upper esophageal sphincter release operation to allow bett |
Completed |
: Study of Muscle Abnormalities in Patients With Specific Genetic Mutations :
|
Active, not recruiting |
: Treatment of Ptosis to Muscular Dystrophy Oculopharyngeal by Myoblast Autologous Graft :
: 2016-03-08 : Biological: Myoblast autologous graft 30 million autologous myoblasts in 6 intramuscular injections No t |
RECRUITING |
: A Study to Evaluate the Safety and Clinical Activity of Intramuscular Doses of BB-301 Administered to Subjects With Oculopharyngeal Muscular Dystrophy With Dysphagia : Oculopharyngeal Muscular Dystrophy : 2024-05-21 : BB-301 is composed of an AAV9 capsid, AAV9PL, which delivers the gene of interest, comprised of a recombinant genome encoding a single RNA transcri |