Lysosomal Storage Diseases - 50 Studies Found
Recruiting |
: Molecular and Cellular Mechanisms of Lysosomal Storage Diseases : Lysosomal Storage Disorders : 2013-11-25 |
Withdrawn |
: Fetal Umbilical Cord Blood (UCB) Transplant for Lysosomal Storage Diseases :
: Biological: ALD-601 ALD-601 is manufactured by Aldagen from the 20% compartment of the selected umbilica |
Enrolling by invitation |
: Genetic Studies of Lysosomal Storage Disorders :
: 1999-11-03 |
Completed |
: The Classification and Cause of Leukodystrophies of Unknown Cause : Lysosomal Storage Disease : 1999-11-03 |
Active, not recruiting |
: Gene Therapy for Metachromatic Leukodystrophy : Lysosomal Storage Disease : 2012-03-16 : Genetic: Autologous CD34+ stem cells transduced with ARSA encoding lentiviral vector Autologous hematopo |
Recruiting |
: Biomarker for Krabbe Disease :
: 2011-08-29 |
Recruiting |
: Biomarker for Pompe Disease :
: 2011-10-21 |
Recruiting |
: Biomarker for Maroteaux-Lamy Disease :
: 2011-10-24 |
Recruiting |
: Biomarker for Morquio Disease :
: 2011-10-21 |
Completed |
: Reduced-Intensity Hematopoietic Stem Cell Transplant for High Risk Lysosomal and Peroxisomal Disorders :
: 2012-06-20 :
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