Gangliosidoses, GM2 - 17 Studies Found
Completed |
: Pyrimethamine as a Treatment for Late-Onset GM2-gangliosidosis (Tay-Sachs and Sandhoff Disease) :
|
Recruiting |
: A Natural History of Late Onset Tay-Sachs Disease : GM2 Gangliosidosis : 2016-07-19 |
Completed |
: Pharmacokinetics and Tolerability of Zavesca® (Miglustat) In Patients With Juvenile GM2 Gangliosidosis : Gangliosidoses GM2 : 2007-01-04 : Drug: miglustat Target dose of 320 mg/m^2/day (divided in 3 doses) will be based on the Body Surface Are |
Completed |
: Pharmacokinetics, Safety and Tolerability of Zavesca (Miglustat) in Patients With Infantile Onset Gangliosidosis: Single and Steady State Oral Doses :
|
Withdrawn |
: A Phase I Study of Pyrimethamine in Patients With GM2 Gangliosidosis :
|
Recruiting |
: Biomarker for GM1/GM2 - Gangliosidoses :
|
Recruiting |
: Synergistic Enteral Regimen for Treatment of the Gangliosidoses :
|
Recruiting |
: A Natural History Study of the Gangliosidoses :
|
Active, not recruiting |
: Efficacy Study of an Online Educational Module Before Carrier Genetic Screening in Persons of Ashkenazi Jewish Descent. :
|
Completed |
: Gene Therapy for Tay-Sachs Disease :
|